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Publications
Peay HL, Fischer R, Mange B, Paquin RS, Smith EC, Sadosky A, Russo L, Ricotti V, Rensch C, Morris C, Martin AS, Ganot A, Beaverson K, Mansfield C . Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy . Mol Genet Genomic Med. 2021 May;9(5):e1664. doi: 10.1002/mgg3.1664
DiBenedetti D , Slota C, Wronski SL, Vradenburg G, Comer M, Callahan LF, Winfield J, Rubino I, Krasa HB, Hartry A, Wieberg D, Kremer IN, Lappin D, Martin AD, Frangiosa T, Biggar V, Hauber B. Assessing what matters most to patients with or at risk for Alzheimer's and care partners: a qualitative study evaluating symptoms, impacts, and outcomes . Alzheimers Res Ther. 2020 Jul 30;12(90). doi: 10.1186/s13195-020-00659-6
Hartry A, Menne H, Wronski S, Paulson R, Callahan L, Potashman M, Lee D, Wunderlich G, Hoffman D, Wieberg D, Kremer I, Hauber B, DiBenedetti D . Evaluation of what matters most in existing clinical outcomes assessments in Alzheimer's Disease . Poster presented at the 2020 Alzheimer's Association Virtual International Conference (AAIC); July 29, 2020.
Hauber B, Paulsen R, Callahan L, Potashman M, Lee D, Hartry A, Wunderlich G, Hoffman D, Wieberg D, Kremer I, DiBenedetti D . Quantifying what matters most to patients and care partners in Alzheimer's Disease . Poster presented at the 2020 Alzheimer's Association Virtual International Conference (AAIC); July 29, 2020.
Majid T, Paulsen R, Callahan L, Potashman M, Lee D, Hartry A, Wunderlich G, Hoffman D, Wieberg D, Kremer I, Hauber B, DiBenedetti D . The importance of care partner input in Alzheimer's Disease (AD) drug development . Poster presented at the 2020 Alzheimer's Association Virtual International Conference (AAIC); July 27, 2020.
Hauber B, DiBenedetti D , Vradenburg G, Callahan L, Potashman M, Krasa H, Hartry A, Wunderlich G, Hoffman D, Wieberg D, Kremer I. Identifying what matters to people with and at risk for Alzheimer's disease and their care partners: concept elicitation and item development . Poster presented at the 12th Clinical Trials in Alzheimer’s Disease (CTAD) Meeting; December 6, 2019. San Diego, CA.
Vradenburg G, DiBenedetti DB , Hauber B, Slota C, Wronski SL, Comer M, Callahan LF, Winfield J, Rubino I, Krasa HB, Hartry A, Wieberg BA, Kremer IN, Lappin D, Martin AD, Frangiosa T, Biggar V. Findings from the Alzheimer' Disease Patient and Caregiver Engagement (AD PACE) initiative's what matters most qualitative study . Poster presented at the 2019 Alzheimer's Association International Conference (AAIC); July 17, 2019. Los Angeles, CA.
Paquin RS, Fischer R, Mansfield C , Mange B, Beaverson K, Ganot A, Martin AS, Morris C, Rensch C, Ricotti V, Russo LJ, Sadosky A, Smith EC, Peay H. Priorities when deciding on participation in early-phase gene therapy trials for Duchenne muscular dystrophy: a best–worst scaling experiment in caregivers and adult patients . Orphanet J Rare Dis. 2019 May 9;14(1):102. doi: 10.1186/s13023-019-1069-6
Peay H, Fischer R, Tzeng JP, Hesterlee SE, Morris C, Martin AS, Rensch C, Smith E, Ricotti V, Beaverson K, Wand H, Mansfield C . Gene therapy as a potential therapeutic option for Duchenne muscular dystrophy: a qualitative preference study of patients and parents . PLoS One. 2019 May 1;14(5):e0213649. doi: 10.1371/journal.pone.0213649
Herring W , Gould IG, Casamassima G, Dort T, Zhang Y, Acosta C, Hyde R, Spelman T, Butzkueven H. A cost-effectiveness analysis using real-world data from the MSBase Registry: comparing natalizumab to fingolimod in patients with inadequate response to disease-modifying therapies in relapsing-remitting multiple sclerosis in Italy . Poster presented at the 2018 ISPOR 21st Annual European Congress; November 12, 2018. Barcelona, Spain. [abstract] Value Health. 2018 Oct; 21(Suppl 3):S338.
Herring W , Gould IG, Ruiz L, Dort T, Zhang Y, Acosta C, Hyde R, Spelman T, Butzkueven H. A cost-effectiveness analysis using real-world data from the MSBase Registry: comparing natalizumab to fingolimod in patients with inadequate response to disease-modifying therapies in relapsing-remitting multiple sclerosis in Spain . Poster presented at the 2018 ISPOR 21st Annual European Congress; November 12, 2018. Barcelona, Spain. [abstract] Value Health. 2018 Oct; 21(Suppl 3):S338.