Naik H, Brown M, Meninger S, Lombardelli S. Patient experience with acute hepatic porphyria before and after long-term givosiran treatment in a qualitative interview study. Mol Genet Metab Rep. 2025 Mar;42:101174. doi: 10.1016/j.ymgmr.2024.101174
Garcia-Albeniz X, Hsu J, Etzioni R, Chan JM, Shi J, Dickerman B, Hernan MA. Prostate-specific antigen screening and prostate cancer mortality: an emulation of target trials in US Medicare. JCO Clin Cancer Inform. 2024 Aug;8:e240094. doi: 10.1200/CCI.24.00094