Garcia-Albeniz X, Hsu J, Etzioni R, Chan JM, Shi J, Dickerman B, Hernan MA. Prostate-specific antigen screening and prostate cancer mortality: an emulation of target trials in US Medicare. JCO Clin Cancer Inform. 2024 Aug;8:e240094. doi: 10.1200/CCI.24.00094
Carrillo N, Malicdan MC, Leoyklang P, Shrader JA, Joe G, Slota C, Perreault J, Heiss JD, Class B, Liu CY, Bradley K, Jodarski C, Ciccone C, Driscoll C, Parks R, Van Wart S, Bayman L, Coffey CS, Quintana M, Berry SM, Huizing M, Gahl WA. Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study. Genet Med. 2021 Nov;23(11):2067-75. doi: 10.1038/s41436-021-01259-x