Naik H, Brown M, Meninger S, Lombardelli S. Patient experience with acute hepatic porphyria before and after long-term givosiran treatment in a qualitative interview study. Mol Genet Metab Rep. 2025 Mar;42:101174. doi: 10.1016/j.ymgmr.2024.101174
Thijssen JJJ, Bregantini D. Costly sequential experimentation and project valuation with an application to health technology assessment. J Econ Dyn Control. 2017 Apr 1;77:202-29. doi: 10.1016/j.jedc.2017.01.016