Skip to main content
Publications
Carrillo N, Malicdan MC, Leoyklang P, Shrader JA, Joe G, Slota C, Perreault J, Heiss JD, Class B, Liu CY, Bradley K, Jodarski C, Ciccone C, Driscoll C, Parks R, Van Wart S, Bayman L, Coffey CS, Quintana M, Berry SM, Huizing M, Gahl WA. Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study. Genet Med. 2021 Nov;23(11):2067-75. doi: 10.1038/s41436-021-01259-x
Hall RE, Tusevljak N, Wu CF, Ibrahim Q, Schulze K, Khan AM, Desai D, Awadalla P, Broet P, Dummer TJB, Hicks J, Tardif JC, Teo KK, Vena J, Lee D, Friedrich M, Anand SS, Tu JV. The Canadian alliance for healthy hearts and minds: how well does it reflect the Canadian population? CJC Open. 2020 Jul 22;2(6):599-609. doi: 10.1016/j.cjco.2020.07.013