Peay HL, Fischer R, Mange B, Paquin RS, Smith EC, Sadosky A, Russo L, Ricotti V, Rensch C, Morris C, Martin AS, Ganot A, Beaverson K, Mansfield C. Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy. Mol Genet Genomic Med. 2021 May;9(5):e1664. doi: 10.1002/mgg3.1664
McKenna SP, Doward LC. How should we measure quality of life in ankylosing spondylitis? Rheumatol Pract. 2008;6(2):12-4.
Julvez J, Forns M, Ribas-Fito N, Mazon C, Torrent M, Garcia-Esteban R, Ellison-Loschmann L, Sunyer J. Psychometric characteristics of the California Preschool Social Competence Scale in a spanish population sample. Early Educ Dev. 2008;19(5):795-815.