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Publications
Peay HL, Fischer R, Mange B, Paquin RS, Smith EC, Sadosky A, Russo L, Ricotti V, Rensch C, Morris C, Martin AS, Ganot A, Beaverson K, Mansfield C. Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy. Mol Genet Genomic Med. 2021 May;9(5):e1664. doi: 10.1002/mgg3.1664
Gomez-Roig MD, Pascal R, Cahuana MJ, Garcia-Algar O, Sebastiani G, Andreu-Fernandez V, Martinez L, Rodriguez G, Iglesia I, Ortiz-Arrabal O, Mesa MD, Cabero MJ, Guerra L, Llurba E, Dominguez C, Zanini MJ, Foraster M, Larque E, Cabanas F, Lopez-Azorin M, Perez A, Loureiro B, Pallas-Alonso CR, Escuder-Vieco D, Vento M. Environmental exposure during pregnancy: influence on prenatal development and early life: a comprehensive review. Fetal Diagn Ther. 2021;48(4):245-57. doi: 10.1159/000514884