Peay HL, Fischer R, Mange B, Paquin RS, Smith EC, Sadosky A, Russo L, Ricotti V, Rensch C, Morris C, Martin AS, Ganot A, Beaverson K, Mansfield C. Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy. Mol Genet Genomic Med. 2021 May;9(5):e1664. doi: 10.1002/mgg3.1664
Rockwood NJ, Jeon M. Estimating complex measurement and growth models using the R package PLmixed. Multivar Behav Res. 2019 Mar;54(2):288-306. doi: 10.1080/00273171.2018.1516541